Private company

Ultragenyx Pharmaceutical

Logo: user grmike vectorized the logo which appears on the corporate website, Public domain, via Wikimedia Commons3

American biopharmaceutical company

Ultragenyx Pharmaceutical Inc. is an American biopharmaceutical company involved in the research and development of novel products for treatment of rare and ultra-rare genetic diseases for which there are typically no approved treatments and high unmet medical need.2 Wikipedia text CC BY-SA 4.0

Last updated Oct 21, 2026.

Overview

Ultragenyx Pharmaceutical Inc. is an American biopharmaceutical company involved in the research and development of novel products for treatment of rare and ultra-rare genetic diseases for which there are typically no approved treatments and high unmet medical need.2